Treatment still closer for LCA: another success

Another breakthrough has been reached with animal gene therapy for LCA. This time the target was the Gucy2D mutation,which causes LCA1 - the first gene discovered to cause Leber’s, in 1997.
Embryos of chickens which would be born blind because of this mutation were injected the healthy gene, and after hatching they could see!

The authors point out that although gene therapy was delivered in utero, this doesn’t rule out that it may work on older patients too, once it is tried on humans.

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Let’s hang in there!! Surely more great news to come in the near future.

Fran