One more LCA trial for RPE65

Great news!
Phase 1 gene therapy clinical trials for Leber's Congenital Amaurosis caused by RPE65 have begun at the University of Pennsylvania and the University of Florida! One volunteer patient has received an injection of genes into the retina of one eye. The injection was performed by Shalesh Kaushal, MD, PhD, assistant
professor of ophthalmology at the University of Florida. Six adults and three children between the ages of 8 and 17 years are scheduled to undergo the procedure at the university over the next year.

This is the second gene therapy trial for RPE65, commencing only a few months after the one currently underway at London’s Moorfields Hospital. It will take a while before results from both trials are disclosed, however if things go well the good news should start to leak out soon.