LCA gene therapy trial: directly from the first participant

After introducing himself on this blog a while ago (and what a big surprise that was!), Billy, the first LCA patient to take part in a gene therapy clinical trial, has joined the LCA mailing list and bravely faced the flood of questions that obviously came his way.

Amber, a member of the LCA list who runs a very interesting and informative site on LCA, has patiently put together Billy’s comments and replies, which are now available on her web site at
http://www.wonderbaby.org/articles/lca-gene-therapy-trials.html

Do read this incredible developing story, and stick around for more!

I personally thank Amber for her work, and once again I thank Billy for being willing to share his experience with all of us.


Fran